Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...

People carrying at least one APOE4 allele have a higher risk of Alzheimer's disease. People who carry two alleles have the highest risk, leading some researchers to suggest that APOE4 homozygotes have ...

Scientists behind the study say that if the harmful influence of the gene could be neutralised, up to three-quarters - and ...

Potentially more than 90% of Alzheimer's disease cases would not occur without the contribution of a single gene (APOE), ...

Potentially more than 90% of Alzheimer's disease cases would not occur without the contribution of a single gene (APOE), ...

Here at MIT Technology Review we’ve been writing about the gene-editing technology CRISPR since 2013, calling it the biggest ...

Victoria Gray spent 34 years battling the debilitating pain of sickle cell disease. Then she volunteered to be the world's first "prototype" for a CRISPR therapy, based on technology invented at UC ...

Pharmacogenetics and pharmacogenomics are increasingly recognised as playing a pivotal role in the advancement of personalised medicine, especially in the ...

An HIV-derived nucleoside therapy now treats rare genetic diseases by restoring mitochondrial DNA and improving muscle ...

GEN’s first virtual event of 2026—we present a group of outstanding researchers and thought-leaders to discuss the latest advances and challenges in delivering genetic therapies.

CGTxchange leverages the combined capabilities of the organizations in an unprecedented way to engage a broad array of potential partners and funders to efficiently identify, evaluate, finance, ...

A preclinical study uncovered a new gene therapy that targets pain centers in the brain while eliminating the risk of ...